Work presented: Innovative methodologies to generate mice expressing in the liver human splicing mutations: good model to test in vivo the efficacy of modified U1snRNAs

Grantee name: Mariana Gonçalves

Conference title: 24th European Study Group on Lysosomal Diseases workshop and Graduate course

Date: 05/09/2022 to 10/09/2022
Location: Lancaster, England (in person)