Info

Full name

Aurelie Goyenvalle

Institution

Inserm-University of Versailles

Country

France

ORCID number

0000-0003-3938-1165

Research Interest (use keywords)

ASOs, splice switching, exon skipping, DMD, preclinical development

Disorder of interest

Neuromuscular disorders, Neurodegenerative disorders, Duchenne muscular dystrophy

Organ/tissue of interest

Muscle, Heart, Brain, Eye, Skin

Model system

Cell culture, Mice, Humans